Rett Sydrome

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Our Research Focus

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Goal 1

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Goal 2

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Treatments In Development

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Nuplazid
Rett Syndrome, Test
In Market
2018
Filing Year
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Nuplazid

Rett Syndrome, Test
In Market
2018
Filing Year
Proin gravida, neque auctor auctor egestas, mi est pharetra nulla, id pellentesque diam eros sed nisi. Pellentesque a risus volutpat, vestibulum nisl sit amet, vestibulum mauris. Nam nec lobortis tellus. Maecenas commodo ante vitae libero porta viverra.

Clinical Trial Details

Lilac Study

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Duration
40-Weeks

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Sample Details
160

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Upcoming Milestones

Market Launch

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milestone 2

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Trifonetide
Rett Syndrome
Preclinical
2022
Expected Filing
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Trifonetide

Rett Syndrome
Preclinical
2022
Expected Filing
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Clinical Trial Details

Lavender Study

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Duration
12-Weeks

Double-blind, randomized, placebo-controlled study

Sample Details
180

Girls and young women ages 5 to 20 years with Rett syndrome

Upcoming Milestones

Milestone

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About Rett Syndrome

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Prevalence

6k – 9k
Patients in the U.S. get Rett Syndrome

( 1 out of 10,000–15,000 female births worldwide)

Symptoms

Typically, between 6 to 18 months of age, patients experience:

  • Abnormal hand movements
  • Unusual eye movements
  • Breathing problems
  • Loss of normal movement
  • Loss of communication ability

Featured Perspectives

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